Research Focus

Research Facilities; NE Affiliate

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1. Safety of ascending doses of AAVrh.10hFXN to treat the cardiac manifestations of Friedreich's ataxia

   Meeting Abstract

   Rosenberg, J. B.; Greco, A.; Zuluaga, C. M.; Gertz, M. L. R, ; Yost-Bido, M.; Gorman, N. C.; Chen, A.; Kooner, V.; De, B. P.; Kaminsky, S. M.; more...
   Molecular Therapy (2023)

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2. Identification of safe and effective intravenous dose of AAVrh.10hFXN to treat the cardiac manifestations of Friedreich's ataxia

   Journal Article

   Munoz-Zuluaga, C.; Gertz, M.; Yost-Bido, M.; Greco, A.; Gorman, N.; Chen, A.; Kooner, V.; Rosenberg, J. B.; De, B. P.; Kaminsky, S. M.; more...
   Human Gene Therapy (2023)

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