Authors: | Rosenberg, J. B.; Greco, A.; Zuluaga, C. M.; Gertz, M. L. R, ; Yost-Bido, M.; Gorman, N. C.; Chen, A.; Kooner, V.; De, B. P.; Kaminsky, S. M.; Arbona, R. J. R.; Martin, H. R.; Monette, S.; Khanna, R.; Crystal, R. G.; Sondhi, D. |
Abstract Title: | Safety of ascending doses of AAVrh.10hFXN to treat the cardiac manifestations of Friedreich's ataxia |
Meeting Title: | 26th Annual Meeting of the American Society of Gene & Cell Therapy (ASGCT) |
Journal Title: | Molecular Therapy |
Volume: | 31 |
Issue: | 4 Suppl. 1 |
Meeting Dates: | 2023 May 16-29 |
Meeting Location: | Los Angeles, CA |
ISSN: | 1525-0016 |
Publisher: | Nature Publishing Group |
Date Published: | 2023-05-01 |
Start Page: | 776 |
Language: | English |
ACCESSION: | WOS:001045144203393 |
PROVIDER: | wos |
DOI: | 10.1016/j.ymthe.2023.04.017 |
Notes: | Meeting Abstract: 1656 -- Source: Wos |