Gene therapy: Charting a future course - Summary of a National Institutes of Health Workshop, April 12, 2013 Journal Article
| Authors: | O'Reilly, M.; Federoff, H. J.; Fong, Y.; Kohn, D. B.; Patterson, A. P.; Ahmed, N.; Asokan, A.; Boye, S. E.; Crystal, R. G.; De Oliveira, S.; Gargiulo, L.; Harper, S. Q.; Ikeda, Y.; Jambou, R.; Montgomery, M.; Prograis, L.; Rosenthal, E.; Sterman, D. H.; Vandenberghe, L. H.; Zoloth, L.; Abedi, M.; Adair, J.; Adusumilli, P. S.; Goins, W. F.; Gray, J.; Monahan, P.; Popplewell, L.; Sena-Esteves, M.; Tannous, B.; Weber, T.; Wierda, W.; Gopal-Srivastava, R.; McDonald, C. L.; Rosenblum, D.; Corrigan-Curay, J. |
| Article Title: | Gene therapy: Charting a future course - Summary of a National Institutes of Health Workshop, April 12, 2013 |
| Abstract: | Recently, the gene therapy field has begun to experience clinical successes in a number of different diseases using various approaches and vectors. The workshop Gene Therapy: Charting a Future Course, sponsored by the National Institutes of Health (NIH) Office of Biotechnology Activities, brought together early and mid-career researchers to discuss the key scientific challenges and opportunities, ethical and communication issues, and NIH and foundation resources available to facilitate further clinical advances. © 2014, Mary Ann Liebert, Inc. |
| Keywords: | unclassified drug; review; interferon; nonhuman; risk benefit analysis; follow up; antineoplastic agent; gene targeting; cancer immunotherapy; microrna; gene expression; cell protein; rna interference; clinical protocol; cell differentiation; food and drug administration; gene transfer; genetic manipulation; viral gene delivery system; diabetes mellitus; cytotoxic t lymphocyte; gene therapy; lentivirus vector; retrovirus vector; transgene; long term care; clinical research; interpersonal communication; muscle disease; immunomodulating agent; pluripotent stem cell; hematopoietic stem cell; adenovirus vector; eye disease; immune deficiency; adaptive immunity; ex vivo study; conceptual framework; neurologic disease; medical ethics; genomic dna; national health organization; scientist; complementary dna; retrovirus; virus vector; hemophilia; plasmid dna; clinical trial (topic); antigen antibody complex; workshop; guanylate cyclase; new drug; recombinant dna; adeno associated virus; human; retina degeneration; muscular dystrophy; gene therapy agent; guanylate cyclase 1; parvovirus vector; biosafety |
| Journal Title: | Human Gene Therapy |
| Volume: | 25 |
| Issue: | 6 |
| ISSN: | 1043-0342 |
| Publisher: | Mary Ann Liebert, Inc |
| Date Published: | 2014-06-20 |
| Start Page: | 488 |
| End Page: | 497 |
| Language: | English |
| DOI: | 10.1089/hum.2014.045 |
| PROVIDER: | scopus |
| PMCID: | PMC4064731 |
| PUBMED: | 24773122 |
| DOI/URL: | |
| Notes: | Export Date: 1 August 2014 -- CODEN: HGTHE -- Source: Scopus |
