Towards the genetic treatment of β-thalassemia: New disease models, new vectors, new cells Journal Article


Authors: Moi, P.; Sadelain, M.
Article Title: Towards the genetic treatment of β-thalassemia: New disease models, new vectors, new cells
Keywords: gene mutation; gene deletion; review; nonhuman; animals; mice; gene expression; anemia; mice, mutant strains; transcription factor; stem cell transplantation; hematopoietic stem cell transplantation; genetic transcription; mice, scid; mice, inbred c57bl; genetic vectors; mice, transgenic; recombinant fusion proteins; gene therapy; lentivirus; globin; beta thalassemia; globin gene; beta-thalassemia; fibroblasts; disease models, animal; mice, inbred nod; bone marrow transplantation; transgenes; globins; cell dedifferentiation; sickle cell anemia; iron overload; hemoglobin synthesis; genes, synthetic
Journal Title: Haematologica
Volume: 93
Issue: 3
ISSN: 0390-6078
Publisher: Ferrata Storti Foundation  
Date Published: 2008-03-01
Start Page: 325
End Page: 330
Language: English
DOI: 10.3324/haematol.12732
PUBMED: 18310536
PROVIDER: scopus
DOI/URL:
Notes: --- - "Cited By (since 1996): 2" - "Export Date: 17 November 2011" - "CODEN: HAEMA" - "Source: Scopus"
Altmetric
Citation Impact
MSK Authors
  1. Paolo Moi
    2 Moi
  2. Michel W J Sadelain
    532 Sadelain