Genome editing technologies: Defining a path to clinic Journal Article


Authors: Corrigan-Curay, J.; O'Reilly, M.; Kohn, D. B.; Cannon, P. M.; Bao, G.; Bushman, F. D.; Carroll, D.; Cathomen, T.; Joung, J. K.; Roth, D.; Sadelain, M.; Scharenberg, A. M.; Von Kalle, C.; Zhang, F.; Jambou, R.; Rosenthal, E.; Hassani, M.; Singh, A.; Porteus, M. H.
Article Title: Genome editing technologies: Defining a path to clinic
Keywords: signal transduction; unclassified drug; sequence analysis; nonhuman; conference paper; cell protein; molecular dynamics; gene function; genome analysis; dna modification; medical research; gene identification; nuclease; zinc finger nuclease; chromosome rearrangement; double stranded dna break; dna sequence; antivirus agent; human immunodeficiency virus; virus load; genomic dna; cytotoxicity assay; gene technology; transcription activator like effector nuclease; process design; human; clustered regularly interspaced short palindromic repeat; cas9 protein; meganuclease; sb 728t; genome editing technology; genotoxicity assay
Journal Title: Molecular Therapy
Volume: 23
Issue: 5
ISSN: 1525-0016
Publisher: Nature Publishing Group  
Date Published: 2015-05-01
Start Page: 796
End Page: 806
Language: English
DOI: 10.1038/mt.2015.54
PROVIDER: scopus
PUBMED: 25943494
PMCID: PMC4427885
DOI/URL:
Notes: Export Date: 3 June 2015 -- Source: Scopus
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  1. Michel W J Sadelain
    584 Sadelain