Childhood-onset Erdheim-Chester disease in the molecular era: Clinical phenotypes and long-term outcomes of 21 patients Research Letter


Authors: Pegoraro, F.; Mazzariol, M.; Trambusti, I.; Bakhshi, S.; Mallick, S.; Dunkel, I. J.; van den Bos, C.; Tezol, Ö; Shan, S.; Ocak, S.; Giordano, F.; De Fusco, C.; Gaspari, S.; Buccoliero, A. M.; Coniglio, M. L.; Buti, E.; Romagnani, P.; Picarsic, J.; Donadieu, J.; Diamond, E. L.; Emile, J. F.; Sieni, E.; Haroche, J.; Vaglio, A.
Title: Childhood-onset Erdheim-Chester disease in the molecular era: Clinical phenotypes and long-term outcomes of 21 patients
Journal Title: Blood
Volume: 142
Issue: 13
ISSN: 0006-4971
Publisher: American Society of Hematology  
Date Published: 2023-09-28
Start Page: 1167
End Page: 1171
Language: English
DOI: 10.1182/blood.2023020569
PUBMED: 37490651
PROVIDER: scopus
DOI/URL:
Notes: The MSK Cancer Center Support Grant (P30 CA008748) is acknowledged in the PDF -- Source: Scopus
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  1. Ira J Dunkel
    371 Dunkel
  2. Eli Louis Diamond
    202 Diamond