Assessment of safety and biodistribution of AAVrh.10hCLN2 following intracisternal administration in nonhuman primates for the treatment of CLN2 Batten disease Meeting Abstract
| Authors: | Sondhi, D.; Rosenberg, J. B.; De, B. P.; Kooner, V.; Wilson, I.; Yusufzai, N.; Kaminsky, S. M.; Arbona, R. J. R.; Monette, S.; Nair, A.; Selvan, N.; Khanna, R.; Barth, J. A.; Crystal, R. G. |
| Abstract Title: | Assessment of safety and biodistribution of AAVrh.10hCLN2 following intracisternal administration in nonhuman primates for the treatment of CLN2 Batten disease |
| Meeting Title: | 29th Annual Congress of the European Society of Gene and Cell Therapy (ESGCT) in collaboration with the British Society for Gene and Cell Therapy (BSGCT) |
| Journal Title: | Human Gene Therapy |
| Volume: | 33 |
| Issue: | 23-24 |
| Meeting Dates: | 2022 Oct 11-14 |
| Meeting Location: | Edinburgh, United Kingdom |
| ISSN: | 1043-0342 |
| Publisher: | Mary Ann Liebert, Inc |
| Date Published: | 2022-12-01 |
| Start Page: | A73 |
| Language: | English |
| ACCESSION: | WOS:000899950600228 |
| PROVIDER: | wos |
| DOI: | 10.1089/hum.2022.29225.abstracts |
| Notes: | Meeting Abstract: P180 -- Source: Wos |
